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Norditropin has received orphan drug designation for the treatment of short stature associated with Noonan syndrome.
诺和诺德人体生长激素已经获得孤儿药指定,以治疗努南综合症引起的身材矮小.
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Sabril was designated as an orphan drug by the FDA for use in treating infantile spasms.
喜保宁被FDA指定为用于治疗婴儿痉挛的稀少药品.
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